Access comprehensive financial analyses and make smarter investments - get the Manual of Investments on Amazon!

FDA lifts clinical hold on Intellia Therapeutics' Nexiguran Ziclumeran trial

Intellia Therapeutics, Inc. has just announced that the U.S. Food and Drug Administration (FDA) has lifted the clinical hold on the investigational new drug application (IND) for the magnitude-2 phase 3 clinical trial of Nexiguran Ziclumeran (Nex-Z) for patients with hereditary transthyretin amyloidosis with polyneuropathy (ATTRv-PN). This comes after the FDA had imposed a clinical hold on the INDs for magnitude and magnitude-2 on October 29, 2025, due to observations of grade 4 liver transaminases and increased total bilirubin in a patient who was dosed with Nex-Z in magnitude.

The company has stated that they have aligned with the FDA on certain study modifications and mitigation measures related to magnitude-2, including enhanced safety monitoring of liver laboratory tests. As a result, Intellia plans to resume patient enrollment and dosing for the magnitude-2 trial as quickly as possible.

As part of the protocol amendment, Intellia has increased the trial's target enrollment from approximately 50 patients to approximately 60 patients with ATTRv-PN. The primary endpoints of the study are a change in modified neuropathy impairment score and a change in serum TTR levels. Adult patients with ATTRv-PN are randomized 1:1 to receive a single 55 mg infusion of Nex-Z or placebo.

Intellia also mentioned that their engagement with the FDA is ongoing regarding the clinical hold on the IND for the magnitude phase 3 clinical trial of Nex-Z for patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM), and the company plans to provide an update once alignment has been achieved on the path forward for this program.

As a result of these announcements, the company's shares have moved 5.31% on the market, and are now trading at a price of $12.50. For more information, read the company's full 8-K submission here.

The above analysis is intended for educational purposes only and was performed on the basis of publicly available data. It is not to be construed as a recommendation to buy or sell any security. Any buy, sell, or other recommendations mentioned in the article are direct quotations of consensus recommendations from the analysts covering the stock, and do not represent the opinions of Market Inference or its writers. Past performance, accounting data, and inferences about market position and corporate valuation are not reliable indicators of future price movements. Market Inference does not provide financial advice. Investors should conduct their own review and analysis of any company of interest before making an investment decision.

IN FOCUS